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Casgevy\u7531\u5236\u836f\u516c\u53f8Vertex Pharmaceuticals\u548c\u751f\u7269\u6280\u672f\u516c\u53f8CRISPR Therapeutics\u5171\u540c\u5f00\u53d1\uff0c\u7528\u4e8e\u6cbb\u759712\u5c81\u53ca\u4ee5\u4e0a\u6210\u4eba\u9570\u72b6\u7ec6\u80de\u75c5\u3002CRISPR Therapeutics\u7531\u8bfa\u8d1d\u5c14\u5956\u83b7\u5f97\u8005Emmanuelle Charpentier\u521b\u7acb\uff0c\u8be5\u7597\u6cd5\u4e0a\u4e2a\u6708\u83b7\u5f97\u4e86\u82f1\u56fd\u76d1\u7ba1\u673a\u6784\u7684\u6279\u51c6\u3002<\/p>\n\n\n\n

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Vertex\u516c\u53f8CEO Reshma Kewalramani\u8868\u793a\uff1a\u201c\u6211\u4eec\u76f8\u4fe1\u836f\u54c1\u7684\u4ef7\u683c\u80fd\u591f\u53cd\u6620\u5176\u5e26\u6765\u7684\u4ef7\u503c\uff0c\u800c\u8fd9\u79cd\u4ef7\u503c\u6240\u5e26\u6765\u7684\u4ef7\u503c\u662f\u4e00\u6b21\u6027\u7597\u6cd5\uff0c\u53ef\u80fd\u7ec8\u751f\u6cbb\u6108\u75be\u75c5\u3002\u201d<\/p>\n\n\n\n

\u4e0e\u6b64\u540c\u65f6\uff0c\u84dd\u9e1f\u516c\u53f8\uff08Bluebird Bio\uff09\u7684\u4e00\u6b3e\u57fa\u56e0\u7597\u6cd5Lyfgenia\u5f53\u5929\u4e5f\u83b7\u5f97\u4e86\u7f8e\u56fdFDA\u6279\u51c6\uff0c\u7528\u4e8e\u6cbb\u759712\u5c81\u53ca\u4ee5\u4e0a\u4eba\u7fa4\u7684\u9570\u72b6\u7ec6\u80de\u75c5\uff0c\u6bcf\u4f4d\u60a3\u8005\u7684\u6cbb\u7597\u8d39\u7528\u66f4\u662f\u9ad8\u8fbe310\u4e07\u7f8e\u5143\u3002<\/p>\n\n\n\n

2012\u5e74\uff0c\u4e24\u4f4d\u5973\u6027\u79d1\u5b66\u5bb6Jennifer Doudna\u548cEmmanuelle Charpentier\u53d1\u8868\u4e86\u5173\u4e8e\u540d\u4e3aCRISPR-Cas9\u7684\u57fa\u56e0\u7f16\u8f91\u7cfb\u7edf\u7684\u5f00\u521b\u6027\u8bba\u6587\uff0c\u5979\u4eec\u968f\u540e\u56e0\u6b64\u83b7\u5f97\u8bfa\u8d1d\u5c14\u5956\u3002<\/p>\n\n\n\n

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